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| Fecha de publicación | Título | Autor(es) | | abr-2016 | Correction of a Recurrent COL7A1 Mutation in Recessive Dystrophic Epidermolysis Bullosa Keratinocytes | Chamorro, C; Mencía, A; Almarza, D; Duarte, B; Büning, H; Sallach, J; Hausser, I; Larcher, F; Murillas, R |
| jun-2018 | Deletion of a Pathogenic Mutation-Containing Exon of COL7A1 Allows Clonal Gene Editing Correction of RDEB Patient Epidermal Stem Cells | Mencía, A; Chamorro, C; Bonafont, J; Duarte, B; Holguin, A; Illera, N; Llames, SG; Escámez, MJ; Hausser, I; del Río, M; Larcher, F; Murillas, R |
| 28-ene-2025 | Targeted gene therapy into a safe harbor site in human hematopoietic progenitor cells | Rodriguez-Fornes, Fatima; Quintana-Bustamante, Oscar; Lozano, MLuz; Segovia, José Carlos; Bueren, Juan A.; Guenechea, Guillermo |
Mostrando resultados 1 a 3 de 3
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