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Buscar por Materia gene editing
Mostrando resultados 1 a 11 de 11
| Fecha de publicación | Título | Autor(es) | | ene-2020 | Advances in the gene therapy of monogenic blood cell diseases | Bueren, J; Quintana-Bustamante, O; Almarza, E; Navarro, S; Rio, P; Segovia, JC; Guenechea, G |
| 28-ene-2025 | Advances in the gene therapy of monogenic blood cell diseases | Bueren, Juan A.; Quintana-Bustamante, Oscar; Almarza, Elena; Navarro, Susana; Rio, Paula; Segovia, José Carlos; Guenechea, Guillermo |
| may-2019 | Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing | Bonafont, J; Mencía, A; García, M; Torres, R; Rodríguez, S; Carretero, M; Chacón-Solano, E; Modamio-Høybjør, S; Marinas, L; León, C; Escámez, MJ; Hausser, I; del Río, M; Murillas, R; Larcher, F |
| abr-2016 | Correction of a Recurrent COL7A1 Mutation in Recessive Dystrophic Epidermolysis Bullosa Keratinocytes | Chamorro, C; Mencía, A; Almarza, D; Duarte, B; Büning, H; Sallach, J; Hausser, I; Larcher, F; Murillas, R |
| jun-2018 | Deletion of a Pathogenic Mutation-Containing Exon of COL7A1 Allows Clonal Gene Editing Correction of RDEB Patient Epidermal Stem Cells | Mencía, A; Chamorro, C; Bonafont, J; Duarte, B; Holguin, A; Illera, N; Llames, SG; Escámez, MJ; Hausser, I; del Río, M; Larcher, F; Murillas, R |
| jun-2022 | Efficient and Fast Generation of Relevant Disease Mouse Models by In Vitro and In Vivo Gene Editing of Zygotes | Sanchez-Baltasar, Raquel; Garcia-Torralba, Aida; Nieto-Romero, Virginia; Page, Angustias; Molinos-Vicente, Andrea; López-Manzaneda, Sergio; Ojeda-Pérez, Isabel; Ramírez, Ángel; Navarro, Manuel; Segovia, José Carlos; García-Bravo, María |
| jun-2020 | Efficient CRISPR-Cas9-Mediated Gene Ablation in Human Keratinocytes to Recapitulate Genodermatoses: Modeling of Netherton Syndrome | Gálvez, V; Chacón-Solano, E; Bonafont, J; Mencía, A; Wei-Li, D; Murillas, R; Llames, S; Vicente, A; del Río, M; Carretero, M; Larcher, F |
| 19-sep-2019 | NHEJ-Mediated Repair of CRISPR-Cas9-Induced DNA Breaks Efficiently Corrects Mutations in HSPCs from Patients with Fanconi Anemia. | Román-Rodríguez, FJ; Ugalde, L; Álvarez, L; Díez, B; Ramírez, MJ; Risueño, C; Cortón, M |
| abr-2022 | Non-viral delivery of CRISPR-Cas9 complexes for targeted gene editing via a polymer delivery system | O'Keeffe Ahern, J; Lara-Saez, I; Zhou, D; Murillas, R; Bonafont, J; Mencía, A; García, M; Manzanares, D; Lynch, J; Foley, R; Qian, X; Sigen, A; Larcher, F; Wang, W |
| sep-2022 | Preclinical model for phenotypic correction of dystrophic epidermolysis bullosa by in vivo CRISPR-Cas9 delivery using adenoviral vectors | García, M; Bonafont, J; Martínez-Palacios, J; Xu, R; Turchiano, G; Svenson, S; Thrasher, AJ; Larcher, F; del Río, M; Hernández-Alcoceba, R; Garín, MI; Mencía, A; Murillas, R |
| 28-ene-2025 | Targeted gene therapy into a safe harbor site in human hematopoietic progenitor cells | Rodriguez-Fornes, Fatima; Quintana-Bustamante, Oscar; Lozano, MLuz; Segovia, José Carlos; Bueren, Juan A.; Guenechea, Guillermo |
Mostrando resultados 1 a 11 de 11
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