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Buscar por Materia gene therapy
Mostrando resultados 1 a 7 de 7
| Fecha de publicación | Título | Autor(es) | | ene-2020 | Advances in the gene therapy of monogenic blood cell diseases | Bueren, J; Quintana-Bustamante, O; Almarza, E; Navarro, S; Rio, P; Segovia, JC; Guenechea, G |
| 28-ene-2025 | Advances in the gene therapy of monogenic blood cell diseases | Bueren, Juan A.; Quintana-Bustamante, Oscar; Almarza, Elena; Navarro, Susana; Rio, Paula; Segovia, José Carlos; Guenechea, Guillermo |
| may-2019 | Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing | Bonafont, J; Mencía, A; García, M; Torres, R; Rodríguez, S; Carretero, M; Chacón-Solano, E; Modamio-Høybjør, S; Marinas, L; León, C; Escámez, MJ; Hausser, I; del Río, M; Murillas, R; Larcher, F |
| jun-2021 | Correction of recessive dystrophic epidermolysis bullosa by homology-directed repair-mediated genome editing | Bonafont, J; Mencía, A; Chacón-Solano, E; Srifa, W; Vaidyanathan, S; Romano, R; García, M; Hervás-Salcedo, R; Ugalde, L; Duarte, B; Porteus, MH; del Río, M; Larcher, F; Murillas, R |
| jun-2018 | Deletion of a Pathogenic Mutation-Containing Exon of COL7A1 Allows Clonal Gene Editing Correction of RDEB Patient Epidermal Stem Cells | Mencía, A; Chamorro, C; Bonafont, J; Duarte, B; Holguin, A; Illera, N; Llames, SG; Escámez, MJ; Hausser, I; del Río, M; Larcher, F; Murillas, R |
| ago-2024 | Identification of novel small molecule-based strategies of COL7A1 upregulation and readthrough activity for the treatment of recessive dystrophic epidermolysis bullosa | Jover, I; Ramos, MC; Escámez, MJ; Lozoya, E; Tormo, JR; de Prado-Verdún, D; Mencía, A; Pont, M; Puig, C; Larraufie, MH; Gutiérrez-Caballero, C; Reyes, F; Trincado, JL; García-Gonzalez, V; Cerrato, R; Andrés, M; Crespo, M; Vicente, F; Godessart, N; Genilloud, O; Larcher, F; Nueda, A |
| sep-2025 | Regulatory Strategies for Accelerating the Translation of Gene Therapies to Clinical Practice: Focus on GMO Considerations | Delgadillo, J; Martín, F; Carmona, G; Canals, JM; Rio, P; Eguizabal, C; Prosper, F |
Mostrando resultados 1 a 7 de 7
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