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Buscar por Autor Segovia, José Carlos
Mostrando resultados 7 a 11 de 11
Fecha de publicación | Título | Autor(es) | 29-jul-2021 | Preclinical studies of efficacy thresholds and tolerability of a clinically ready lentiviral vector for pyruvate kinase deficiency treatment | Navarro, Susana; Quintana-Bustamante, Óscar; Sánchez-Domínguez, Rebeca; López-Manzaneda, Sergio; Ojeda-Pérez, Isabel; García-Torralba, Aida; Alberquilla, Omaira; Law, Kenneth; Beard, Brian C; Bastone, Antonella; Rothe, Michael; Villanueva, Mariela; Ramírez, Juan Carlos; Fañanas-Baquero, Sara; Nieto-Romero, Virginia; Molinos-Vicente, Andrea; Gutiérrez, Sonia; Nicoletti, Eileen; García-Bravo, María; Bueren, Juan Antonio; Schwartz, Jonathan D; Segovia, José Carlos |
24-abr-2024 | Restored glyoxylate metabolism after AGXT gene correction and direct reprogramming of primary hyperoxaluria type 1 fibroblasts | Nieto-Romero, Virginia; García-Torralba, Aida; Molinos-Vicente, Andrea; Moya, Francisco José; García-Escudero, Ramón; Salido, Eduardo; Segovia, José Carlos; García-Bravo, María |
ago-2016 | Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency | García-Gómez, María; Calabria, Andrea; García-Bravo, María; Benedicenti, Fabrizio; Kosinski, Penelope; López-Manzaneda, Sergio; Hill, Collin; Mañu-Pereira, María del Mar; Martín, Miguel Ángel; Orman, Israel; Vives-Corrons, Joan Lluis; Kung, Charles; Schambach, Axel; Jin, Shengfang; Bueren, Juan Antonio; Montini, Eugenio; Navarro, Susana; Segovia, José Carlos |
jul-2016 | Silencing of hepatic fate-conversion factors induce tumorigenesis in reprogrammed hepatic progenitor-like cells | Serrano, Felipe; García-Bravo, María; Blázquez, Marina; Torres, Josema; Castell, Jose V; Segovia, José Carlos; Bort, Roque |
ago-2023 | Soluble mutant huntingtin drives early human pathogenesis in Huntington's disease | Miguez, Andrés; Gomis, Cinta; Vila, Cristina; Monguió-Tortajada, Marta; Fernández-García, Sara; Bombau, Georgina; Galofré, Mireia; García-Bravo, María; Sanders, Phils; Fernández-Medina, Helena; Poquet, Blanca; Salado-Manzano, Cristina; Roura, Santiago; Alberch, Jordi; Segovia, José Carlos; Allen, Nicholas D.; Borràs, Francesc E.; Canals, Josep M. |
Mostrando resultados 7 a 11 de 11
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